USD 7.63 billion
Hemoglobinopathies Treatment Market Size, Share, Growth Analysis, By Treatment(Stem cell therapy, blood transfusion, iron chelation therapy and others), By Application(Thalassemia, sick cell anaemia and others), By Region - Industry Forecast 2024-2031
Report ID:
SQMIG35H2230 |
Region:
Global |
Published Date: February, 2024
Pages:
157
|Tables:
62
|Figures:
75
Hemoglobinopathies Treatment Market Insights
Hemoglobinopathies Treatment Market size was valued at USD 8.32 billion in 2022 and is poised to grow from USD 9.07 billion in 2023 to USD 18.07 billion by 2031, at a CAGR of 9% during the forecast period (2024-2031).
The global hemoglobinopathies treatment market is a rapidly growing sector that encompasses a wide range of therapeutic approaches and solutions aimed at managing and treating hemoglobinopathies, including sickle cell disease (SCD) and thalassemia. Hemoglobinopathies are a group of inherited blood disorders characterized by abnormalities in the structure or production of hemoglobin, leading to various complications and symptoms. The market is witnessing significant advancements in treatment options, including gene therapy, stem cell transplantation, and novel drug therapies. These innovative treatments offer the potential to address the underlying genetic defects, alleviate symptoms, and improve the quality of life for patients. The market is also experiencing a surge in research and development activities, collaborations, and strategic partnerships to accelerate the development of novel therapies and bring them to the market.
Additionally, increasing awareness about these disorders, supportive government initiatives, and improved healthcare infrastructure in emerging economies are driving market growth. However, challenges such as high treatment costs, limited accessibility to advanced therapies in certain regions, and the need for specialized healthcare professionals pose obstacles to market expansion. Overall, the global market is poised for substantial growth, driven by ongoing research, technological advancements, and a growing emphasis on personalized medicine approaches to address the unmet needs of patients with hemoglobinopathies.
Market Snapshot - 2024-2031
Global Market Size
Largest Segment
Blood Transfusion
Fastest Growth
Blood Transfusion
Growth Rate
9% CAGR
Global Hemoglobinopathies Treatment Market ($ Bn)
Country Share for North America Region (%)
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Hemoglobinopathies Treatment Market Segmental Analysis
Global Hemoglobinopathies Treatment Market is segmented on the basis of treatment, application and region. By treatment, the market is segmented into Stem cell therapy, blood transfusion, iron chelation therapy and others. By application, the market is segmented into Thalassemia, sick cell anaemia and others. By region, the market is segmented into North America, Europe, Asia Pacific, Middle East and Africa, and Latin America.
Analysis By Treatment
The dominant segment in the global hemoglobinopathies treatment market is blood transfusion. Blood transfusion plays a crucial role in managing hemoglobinopathies by replenishing healthy red blood cells and alleviating symptoms associated with anemia. It is a well-established and widely adopted treatment approach for conditions such as thalassemia and sickle cell disease. Blood transfusion helps in maintaining hemoglobin levels, reducing the frequency and severity of complications, and improving overall quality of life for patients. The availability and accessibility of blood transfusion services, along with advancements in blood banking and transfusion technologies, contribute to the dominance of this segment in the market.
The fastest growing segment in the global hemoglobinopathies treatment market is stem cell therapy. Stem cell therapy holds immense promise for treating hemoglobinopathies by providing a curative approach that addresses the root cause of the disorders. It involves the transplantation of healthy stem cells, either from a compatible donor (allogeneic) or the patient's own modified stem cells (autologous), to replace the diseased or dysfunctional cells. Stem cell therapy offers the potential for long-term disease modification, reduced reliance on blood transfusions, and improved overall outcomes for patients. Ongoing research and clinical trials exploring gene therapy and gene editing techniques have further accelerated the development of innovative stem cell-based treatments, driving the rapid growth of this segment in the market.
Analysis By Application
The dominant segment in the global hemoglobinopathies treatment market is thalassemia. Thalassemia is a genetic disorder characterized by abnormal hemoglobin production, leading to severe anemia. It is a significant public health concern in many regions worldwide. The dominant position of the thalassemia segment can be attributed to the high prevalence of thalassemia cases globally, especially in regions such as Southeast Asia, the Mediterranean, and the Middle East. The treatment landscape for thalassemia includes blood transfusions, iron chelation therapy, and emerging therapies like gene therapy and stem cell transplantation. The focus on thalassemia research, the availability of treatment options, and supportive government initiatives contribute to the dominance of this segment in the market.
The fastest growing segment in the global hemoglobinopathies treatment market is sickle cell anemia. Sickle cell anemia is a hereditary blood disorder characterized by the abnormal shape of red blood cells, leading to various complications such as pain crises, organ damage, and reduced life expectancy. The fastest-growing segment status can be attributed to several factors, including increasing awareness about sickle cell anemia, improved diagnosis, and a growing emphasis on developing targeted therapies. There has been a notable surge in research and development efforts to develop innovative treatments for sickle cell anemia, including gene therapies, gene editing techniques, and novel drug therapies. Additionally, advancements in supportive care measures, including pain management and preventive strategies, contribute to the rapid growth of this segment in the market.
Global Hemoglobinopathies Treatment Market By Treatment
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Hemoglobinopathies Treatment Market Regional Insights
North America dominated the global hemoglobinopathies treatment market. North America holds the largest market share due to factors such as a well-established healthcare infrastructure, high healthcare expenditure, and strong research and development activities. The region is witnessing significant advancements in hemoglobinopathies treatment, including the introduction of innovative therapies and targeted drug developments. Additionally, supportive government initiatives, favorable reimbursement policies, and a high prevalence of hemoglobinopathies contribute to the dominance of North America in the global market.
The fastest growing region in the global hemoglobinopathies treatment market is Asia Pacific. The Asia Pacific region is experiencing rapid growth due to several factors, including the high prevalence of hemoglobinopathies, especially thalassemia, in countries like India, Pakistan, and Southeast Asian nations. Increased awareness, improved healthcare infrastructure, rising healthcare spending, and growing investments in research and development activities are driving the growth of this segment. Additionally, collaborations between regional governments, healthcare organizations, and pharmaceutical companies are fostering the development and accessibility of advanced hemoglobinopathies treatments in the Asia Pacific region.
Global Hemoglobinopathies Treatment Market By Geography
- Largest
- Fastest
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Hemoglobinopathies Treatment Market Dynamics
Drivers
Increasing focus on personalized medicine approaches
- One key driver of the global hemoglobinopathies treatment market is the increasing focus on personalized medicine approaches. Personalized medicine aims to tailor treatment strategies based on individual patient characteristics, including their genetic makeup, disease severity, and response to therapy. With advancements in genetic testing and molecular diagnostics, healthcare providers are able to better understand the specific genetic mutations and abnormalities underlying hemoglobinopathies. This knowledge enables the development of targeted therapies and precision medicine interventions that can improve treatment outcomes and patient satisfaction. The emphasis on personalized medicine not only enhances the effectiveness of hemoglobinopathies treatment but also promotes the development of innovative therapeutic options.
Restraints
High cost of advanced therapies
- A key restraint of the global hemoglobinopathies treatment market is the high cost of advanced therapies. Many of the emerging treatment modalities, such as gene therapy and stem cell transplantation, involve complex procedures, specialized equipment, and extensive follow-up care. These factors contribute to the high cost associated with these treatments, making them financially burdensome for patients and healthcare systems. The affordability and accessibility of advanced therapies pose challenges, particularly in regions with limited healthcare resources and lower income populations. The high cost of treatment limits the widespread adoption of novel therapies, potentially hindering patient access and leading to disparities in healthcare outcomes for individuals with hemoglobinopathies. Addressing the cost barrier is crucial to ensure equitable access to effective treatments for all patients
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Hemoglobinopathies Treatment Market Competitive Landscape
The competitive landscape of the global hemoglobinopathies treatment market is characterized by intense competition and the presence of numerous key players. The market is witnessing significant research and development activities, strategic collaborations, and product innovations aimed at gaining a competitive edge. Key players are focusing on expanding their product portfolios, developing advanced therapies, and improving treatment outcomes for patients with hemoglobinopathies. The market is also witnessing increased efforts towards the development of personalized medicine approaches, including gene therapies and targeted drug interventions. Additionally, market players are actively engaged in geographic expansion, market penetration in emerging economies, and collaborations with healthcare organizations to enhance their market presence and cater to the growing demand for effective hemoglobinopathies treatment solutions.
Top Player’s Company Profiles
- Sanofi S.A. (France)
- Global Blood Therapeutics, Inc. (US)
- bluebird bio, Inc. (US)
- EMI Holding, Inc. (US)
- Celgene Corporation (US)
- Novartis AG (Switzerland)
- Gilead Sciences, Inc. (US)
- CRISPR Therapeutics AG (Switzerland)
- Sangamo Therapeutics, Inc. (US)
- Vertex Pharmaceuticals Incorporated (US)
- Pfizer Inc. (US)
- Bioverativ Inc. (US)
- Acceleron Pharma Inc. (US)
- Agios Pharmaceuticals, Inc. (US)
- Gamida Cell Ltd. (Israel)
- Orchard Therapeutics plc (UK)
- Emmaus Life Sciences, Inc. (US)
- Pharmacosmos A/S (Denmark)
- Fresenius SE & Co. KGaA (Germany)
- Bluebird R&D Spain SLU (Spain)
Recent Developments
- In September 2021, Sanofi announced positive results from the Phase 1/2 trial of its investigational gene therapy for sickle cell disease, demonstrating sustained improvements in hemoglobin levels and reduction in disease-related complications.
- In July 2021, Global Blood Therapeutics received accelerated approval from the U.S. FDA for Oxbryta (voxelotor), an oral therapy for the treatment of sickle cell disease in adults and pediatric patients aged 12 years and older.
- In February 2021, bluebird bio announced that the European Medicines Agency (EMA) had accepted its Marketing Authorization Application (MAA) for LentiGlobin, a gene therapy for transfusion-dependent β-thalassemia, and initiated the review process.
Hemoglobinopathies Treatment Key Market Trends
- Growing emphasis on gene therapy: One key market trend in the global hemoglobinopathies treatment market is the growing emphasis on gene therapy. Gene therapy has emerged as a promising approach for the treatment of hemoglobinopathies, including sickle cell disease and thalassemia. The advancements in genetic engineering techniques, such as CRISPR/Cas9, have provided new possibilities for correcting the genetic mutations underlying these disorders. Gene therapy offers the potential to address the root cause of hemoglobinopathies by introducing functional genes or modifying the existing genes to restore normal hemoglobin production. The increasing research and development activities in gene therapy, along with the successful clinical trials and regulatory approvals, highlight the significant market trend towards this innovative treatment modality.
Hemoglobinopathies Treatment Market SkyQuest Analysis
SkyQuest’s ABIRAW (Advanced Business Intelligence, Research & Analysis Wing) is our Business Information Services team that Collects, Collates, Correlates, and Analyzes the Data collected by means of Primary Exploratory Research backed by robust Secondary Desk research.
According to our Global Hemoglobinopathies Treatment Market analysis, the global market is experiencing rapid growth and significant advancements in therapeutic approaches. Hemoglobinopathies, including sickle cell disease and thalassemia, are genetic blood disorders that require effective management and treatment. The market is driven by factors such as increasing focus on personalized medicine, advancements in gene therapy, and growing investments in research and development activities. Blood transfusion remains the dominant treatment segment, while stem cell therapy is the fastest growing segment due to its potential for curative interventions. North America leads the market, benefiting from a robust healthcare infrastructure and research initiatives. However, the high cost of advanced therapies poses a restraint. Key players are engaged in product development, collaborations, and geographic expansion to cater to the growing demand for effective hemoglobinopathies treatment solutions. The market trend towards gene therapy reflects the potential of genetic engineering techniques to address the root cause of hemoglobinopathies. Overall, the market is poised for substantial growth, with a focus on improving treatment outcomes and enhancing patient access to advanced therapies.
| Report Metric | Details |
|---|---|
| Market size value in 2022 | USD 8.32 billion |
| Market size value in 2031 | USD 18.07 billion |
| Growth Rate | 9% |
| Base year | 2023 |
| Forecast period | 2024-2031 |
| Forecast Unit (Value) | USD Billion |
| Segments covered |
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| Regions covered | North America (US, Canada), Europe (Germany, France, United Kingdom, Italy, Spain, Rest of Europe), Asia Pacific (China, India, Japan, Rest of Asia-Pacific), Latin America (Brazil, Rest of Latin America), Middle East & Africa (South Africa, GCC Countries, Rest of MEA) |
| Companies covered |
|
| Customization scope | Free report customization with purchase. Customization includes:-
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Table Of Content
Executive Summary
Market overview
- Exhibit: Executive Summary – Chart on Market Overview
- Exhibit: Executive Summary – Data Table on Market Overview
- Exhibit: Executive Summary – Chart on Hemoglobinopathies Treatment Market Characteristics
- Exhibit: Executive Summary – Chart on Market by Geography
- Exhibit: Executive Summary – Chart on Market Segmentation
- Exhibit: Executive Summary – Chart on Incremental Growth
- Exhibit: Executive Summary – Data Table on Incremental Growth
- Exhibit: Executive Summary – Chart on Vendor Market Positioning
Parent Market Analysis
Market overview
Market size
- Market Dynamics
- Exhibit: Impact analysis of DROC, 2021
- Drivers
- Opportunities
- Restraints
- Challenges
- Exhibit: Impact analysis of DROC, 2021
- SWOT Analysis
KEY MARKET INSIGHTS
- Technology Analysis
- (Exhibit: Data Table: Name of technology and details)
- Pricing Analysis
- (Exhibit: Data Table: Name of technology and pricing details)
- Supply Chain Analysis
- (Exhibit: Detailed Supply Chain Presentation)
- Value Chain Analysis
- (Exhibit: Detailed Value Chain Presentation)
- Ecosystem Of the Market
- Exhibit: Parent Market Ecosystem Market Analysis
- Exhibit: Market Characteristics of Parent Market
- IP Analysis
- (Exhibit: Data Table: Name of product/technology, patents filed, inventor/company name, acquiring firm)
- Trade Analysis
- (Exhibit: Data Table: Import and Export data details)
- Startup Analysis
- (Exhibit: Data Table: Emerging startups details)
- Raw Material Analysis
- (Exhibit: Data Table: Mapping of key raw materials)
- Innovation Matrix
- (Exhibit: Positioning Matrix: Mapping of new and existing technologies)
- Pipeline product Analysis
- (Exhibit: Data Table: Name of companies and pipeline products, regional mapping)
- Macroeconomic Indicators
COVID IMPACT
- Introduction
- Impact On Economy—scenario Assessment
- Exhibit: Data on GDP - Year-over-year growth 2016-2022 (%)
- Revised Market Size
- Exhibit: Data Table on Hemoglobinopathies Treatment Market size and forecast 2021-2027 ($ million)
- Impact Of COVID On Key Segments
- Exhibit: Data Table on Segment Market size and forecast 2021-2027 ($ million)
- COVID Strategies By Company
- Exhibit: Analysis on key strategies adopted by companies
MARKET DYNAMICS & OUTLOOK
- Market Dynamics
- Exhibit: Impact analysis of DROC, 2021
- Drivers
- Opportunities
- Restraints
- Challenges
- Exhibit: Impact analysis of DROC, 2021
- Regulatory Landscape
- Exhibit: Data Table on regulation from different region
- SWOT Analysis
- Porters Analysis
- Competitive rivalry
- Exhibit: Competitive rivalry Impact of key factors, 2021
- Threat of substitute products
- Exhibit: Threat of Substitute Products Impact of key factors, 2021
- Bargaining power of buyers
- Exhibit: buyers bargaining power Impact of key factors, 2021
- Threat of new entrants
- Exhibit: Threat of new entrants Impact of key factors, 2021
- Bargaining power of suppliers
- Exhibit: Threat of suppliers bargaining power Impact of key factors, 2021
- Competitive rivalry
- Skyquest special insights on future disruptions
- Political Impact
- Economic impact
- Social Impact
- Technical Impact
- Environmental Impact
- Legal Impact
Market Size by Region
- Chart on Market share by geography 2021-2027 (%)
- Data Table on Market share by geography 2021-2027(%)
- North America
- Chart on Market share by country 2021-2027 (%)
- Data Table on Market share by country 2021-2027(%)
- USA
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Canada
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Europe
- Chart on Market share by country 2021-2027 (%)
- Data Table on Market share by country 2021-2027(%)
- Germany
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Spain
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- France
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- UK
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Rest of Europe
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Asia Pacific
- Chart on Market share by country 2021-2027 (%)
- Data Table on Market share by country 2021-2027(%)
- China
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- India
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Japan
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- South Korea
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Rest of Asia Pacific
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Latin America
- Chart on Market share by country 2021-2027 (%)
- Data Table on Market share by country 2021-2027(%)
- Brazil
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Rest of South America
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Middle East & Africa (MEA)
- Chart on Market share by country 2021-2027 (%)
- Data Table on Market share by country 2021-2027(%)
- GCC Countries
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- South Africa
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
- Rest of MEA
- Exhibit: Chart on Market share 2021-2027 (%)
- Exhibit: Market size and forecast 2021-2027 ($ million)
KEY COMPANY PROFILES
- Competitive Landscape
- Total number of companies covered
- Exhibit: companies covered in the report, 2021
- Top companies market positioning
- Exhibit: company positioning matrix, 2021
- Top companies market Share
- Exhibit: Pie chart analysis on company market share, 2021(%)
- Total number of companies covered
Methodology
For the Hemoglobinopathies Treatment Market, our research methodology involved a mixture of primary and secondary data sources. Key steps involved in the research process are listed below:
1. Information Procurement: This stage involved the procurement of Market data or related information via primary and secondary sources. The various secondary sources used included various company websites, annual reports, trade databases, and paid databases such as Hoover's, Bloomberg Business, Factiva, and Avention. Our team did 45 primary interactions Globally which included several stakeholders such as manufacturers, customers, key opinion leaders, etc. Overall, information procurement was one of the most extensive stages in our research process.
2. Information Analysis: This step involved triangulation of data through bottom-up and top-down approaches to estimate and validate the total size and future estimate of the Hemoglobinopathies Treatment Market.
3. Report Formulation: The final step entailed the placement of data points in appropriate Market spaces in an attempt to deduce viable conclusions.
4. Validation & Publishing: Validation is the most important step in the process. Validation & re-validation via an intricately designed process helped us finalize data points to be used for final calculations. The final Market estimates and forecasts were then aligned and sent to our panel of industry experts for validation of data. Once the validation was done the report was sent to our Quality Assurance team to ensure adherence to style guides, consistency & design.
Analyst Support
Customization Options
With the given market data, our dedicated team of analysts can offer you the following customization options are available for the Hemoglobinopathies Treatment Market:
Product Analysis: Product matrix, which offers a detailed comparison of the product portfolio of companies.
Regional Analysis: Further analysis of the Hemoglobinopathies Treatment Market for additional countries.
Competitive Analysis: Detailed analysis and profiling of additional Market players & comparative analysis of competitive products.
Go to Market Strategy: Find the high-growth channels to invest your marketing efforts and increase your customer base.
Innovation Mapping: Identify racial solutions and innovation, connected to deep ecosystems of innovators, start-ups, academics, and strategic partners.
Category Intelligence: Customized intelligence that is relevant to their supply Markets will enable them to make smarter sourcing decisions and improve their category management.
Public Company Transcript Analysis: To improve the investment performance by generating new alpha and making better-informed decisions.
Social Media Listening: To analyze the conversations and trends happening not just around your brand, but around your industry as a whole, and use those insights to make better Marketing decisions.
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